Rectify

Rectify is developing Positive Functional Modulators (PFMs), disease-modifying precision therapeutics that restore ABC transporter function for patients with serious genetic diseases.

ABC transporters are a 48-member family of membrane-bound proteins with etiologic loss-of-function mutations in multiple organ systems and therapeutic areas including the lungs, liver, gastrointestinal tract, eye, and central nervous system.

Headquarters Cambridge, MA
Website rectifypharma.com
Pipeline Preclinical
Twitter @RectifyPharma
LinkedIn RectifyPharma